Agenda

24th Workshop of the EURORDIS Round Table of Companies: "Bringing solutions to young rare disease patients"

September 27, 2016

Barcelona, Spain

Organized by:

EURORDIS Rare Diseases Europe

Location:

Fundació Doctor Robert
Casa Convalescència
Universitat Autònoma de Barcelona
C/Sant Antoni Maria Claret, 171 (corner of Sant Quinti)
Barcelona, Spain

Attendance at this event is limited to corporate representatives from EURORDIS’ Round Table of Companies’ members, or by invitation only.

This interactive meeting will look back at experience gained specifically in the field of rare diseases since the launch of the paediatric regulation in 2006. The impact of the legislation and development of products for children affected by rare diseases will be presented.

Participants will then discuss how this regulation could bring more solutions to young rare disease patients through potential improvements such as:

  • Increased training and engagement of parents and young patients (conditions of success and type of training needed)
  • How Extrapolation and design of Small Population Clinical Trials (SPCTs) can help
  • How to make PIP work for rare diseases? What can industry do to perform more studies on children?
     

 

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